Surgical management of Chiari malformation type 1 associated to MCAP syndrome and study of cerebellar and adjacent tissues for PIK3CA mosaicism.

Fiche publication


Date publication

décembre 2022

Journal

European journal of medical genetics

Auteurs

Membres identifiés du Cancéropôle Est :
Pr FAIVRE Laurence, Pr VABRES Pierre, Pr THAUVIN-ROBINET Christel, Pr KUENTZ Paul


Tous les auteurs :
Di Rocco F, Licci ML, Garde A, Mottolese C, Thauvin-Robinet C, Chevarin M, Guibaud L, Vabres P, Kuentz P, Faivre L

Résumé

Subjects with Megalencephaly-Capillary Malformation-Polymicrogyria syndrome (MCAP) can present with a Chiari Malformation Type 1 and resulting alterations in cerebrospinal fluid (CSF) dynamics, which may require surgical treatment. The aim of this paper is to describe the features of children with MCAP who underwent surgical decompression for CM1, and to explore the PIK3CA variant allele frequency (VAF) identified in cerebellar parenchyma and other adjacent structures.

Mots clés

Cerebellar ectopia, Cerebrospinal fluid, Hydrocephalus, MCAP, PIK3CA, Physiopathology, Suboccipital decompression, Syringomyelia

Référence

Eur J Med Genet. 2022 12 8;:104678